This can be done through different methods such as viral vectors or gene editing tools like CRISPR/Cas9. By introducing a functional copy of the gene, the cells can produce the necessary protein or enzyme that is missing or defective due to the original gene mutation. This can help to correct the underlying genetic cause of a disease and potentially restore normal function to the affected cells. Response area is a promising approach for treating genetic disorders and has shown potential in various preclinical and clinical studies.
